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AVXS‐101 by AveXis, Novartis

Comparison of AVXS-101/ZOLGENSMA relative to nusinersen/spinraza for treatment of infants with spinal muscular atrophy type 1 (SMA Type I)

The first clinical trials between AVXS-101 and nusinersen/spinraza showed which treatment effects in infants with SMA type 1 Both therapies have demonstrated significant improvements in…