Boy with SMA Type 2 is running, standing , sitting, lifting alone under Spinraza

This is a miracle 💓 Boy with SMA Type 2 is running, standing and sitting, lifting alone. This is only possible with early treatment from birth with Spinraza. This is the new face from spinal muscular atrophy (SMA) 💪 #AdgangTilSpinrazaForAlle #AccessToSpinraza

Typical brothers playing. But can you believe one of them has SMA? Gabriel Peters was given the first FDA approved SMA treatment, Spinraza, while it was still in clinical trial three years ago. And this, friends, is a miracle. He is a miracle. The Peters family know this firsthand as their older daughter has SMA Type 2. Typically, the severity (or the type) is similar between siblings. But, with a treatment from birth, doctors now say Gabriel genetically has SMA but is asymptomatic — no type at all. Running, standing, lifting and throwing toys… all things not usually possible with this disease. This is SMA. The new SMA. And it is astounding! NEVER GIVE UP. #thisissma #miraclesdohappen #withalotofwork

Gepostet von Gwendolyn Strong Foundation am Mittwoch, 23. Mai 2018

Congratulations to Magnus, he will be treat with Spinraza in another country

In his own country (Denmark), he was denied access to the only treatment for spinal muscular atrophy.

Now having the parents a positive message. Her son Magnus 17 years old is being treated with Spinraza in Belgium. He has now received the 2 injection via lumbar puncture. He feels already the first improvements into the legs.

With Spinraza can treated adults as well. Countries like Germany have for all SMA types approved without age limit.

Latest study from Germany show. Spinraza works in children and adults

Latest results from the evaluation of Children with SMA Type 1 Under Treatment with Nusinersen within the EAP in Germany

Happy Mothers Day – Julie Cini has finally acheived her dream

This is the story of a strongest mother whose life was not so good for Julie, she lost her husband. Later her daughters to the Genetic Killer number #1, that´s called Spinal Muscular Atrophy or SMA. It’s the story of founder Julie Cini of SMA Australia. After many many years there is finally a treatment there. Spinraza is just the beginning, new treatments are under development

Happy Mothers day for all SMA Mothers 💕 especially to Julie 🌷💕