Safety of intrathecal treatment with nusinersen therapy with SMA

Safety of intrathecal treatment with nusinersen therapy with spinal muscular atrophy SMA Typ 2/3 New study from University Essen shows great results University Essen treated a total of 28 adult SMA patients (9 patients with SMA type 2 and 19 patients with SMA type 3) aged between 18–61 years with nusinersen…. Att fortsätt läsa

Latest results from the evaluation of Children with SMA Type 1 Under Treatment with Nusinersen within the EAP in Germany

Germany has a very large management in the treatment of patients with SMA treated with Spinraza. Germany has the most centrens in Europe , which offering treatment with Spinraza. Of course, this also benefits the research. Now going online the latest evaluations In Germany, treatment with nusinersen was provided to… Att fortsätt läsa

SMA: A treatment is there, but not for everyone

Why aren’t children and adults with rare disease getting access to treatment, this is a good question. Miles was diagnosed with the disease when he was just 13 months old. His parents knew that something was not commonplace, because he had not started to crawl and seemed to be weaker… Att fortsätt läsa