Comparison of AVXS-101/ZOLGENSMA relative to nusinersen/spinraza for treatment of infants with spinal muscular atrophy type 1 (SMA Type I)

The first clinical trials between AVXS-101 and nusinersen/spinraza showed which treatment effects in infants with SMA type 1

Both therapies have demonstrated significant improvements in survival, motor function in patients with spinal muscular atrophy. The indirect comparison in the current study potentially suggests that AVXS-101 may be associated with greater clinical benefits than what was observed for nusinersen.

Compared with nusinersen, AVXS-101 appears to have favorable efficacy outcomes across survival, motor function, and motor milestones.

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NCT02122952
NCT02193074

#Spinraza #ENDEAR #ZOLGENSMA

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Liz

Until those day, was my kiss of death been stronger than those of the devil. I like to ride through hellfire with him ,when I come out victorious afterwards. I'm strong and proud rheumatoid arthritis warrior Följ mig, tack! Liz - Fotoblogg Spelblogg

En kommentar till “Comparison of AVXS-101/ZOLGENSMA relative to nusinersen/spinraza for treatment of infants with spinal muscular atrophy type 1 (SMA Type I)”

  1. A really interesting study, I’ve always known that the day is coming to test the effectiveness of a drug. 😉

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