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Latest Update of SMA drug pipeline is now available

The latest version includes 23 active programs, including two approved therapies, Spinraza in all over the world and Zolgensma® in U.S

Learn more and visit CureSMA
Updated SMA Drug Pipeline Now Available
Therapeutic Approaches

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Light a candle, let it burn. 🕯 Never give up the hope, let the darkness disapear. 🌅 Had a son with X-Linked Spinal Muscular Atrophy (SMAX2)