Kategorier
SMA

New Data to the SHINE open-label extension study

Biogen releases new data from the Shine study (NCT02594124). The has enrolled 292 patients (infants through teenagers) from five previous SPINRAZA clinical studies, including ENDEAR. New findings from the SHINE study show treatment with SPINRAZA resulted in motor function improvement or disease stabilization in toddlers, children and young adults who were treated continuously, some for up to six and a half years.

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Av Mia

Light a candle, let it burn. 🕯 Never give up the hope, let the darkness disapear. 🌅 Had a son with X-Linked Spinal Muscular Atrophy (SMAX2)