Over 800 SMA participant enrolled in Nusinersen EAP Program

We looking back on one of the legendary open clinical trials all time The Nusinersen EAP is one of the largest and most successful in the history of rare diseases. Biogen showed exemplary, how well his gene therapy works. For many children and parents it was the only chance to save the lives of their … Fortsätt läsa Over 800 SMA participant enrolled in Nusinersen EAP Program