SMA TYPE I , II, III – Clinical Trials with RG7916

Spinraza was the beginning. Roche is in the development of a small molecule named RG7916 a new therapy for SMA. ‘Hope with Roche #SMA #SpinalMuskelAtrofi

Clinical Trials with RG7916 by Roche

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FIREFISH TRIAL FOR SMA TYPE 1
https://www.pioneeringhealthcare.com/sma/clinical-trial-sma-type-1/

A NEW TOOL FOR TRACKING THE PROGRESSION OF SPINAL MUSCULAR ATROPHY (SMA): QUANTITATIVE MAGNETIC RESONANCE IMAGING (QMRI).

https://www.pioneeringhealthcare.com/about/sma/new-tool-tracking-progression-spinal-muscular-atrophy-sma-quantitative-magnetic-resonance-imaging-qmri/

Community Update 08-08-2017
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Community Update 15-08-2017
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Community Update 12-10-2017
Roche released a new community update on the SUNFISH trial for SMA Types 2 + 3
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Community Update 15-3-2018
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SMN protein increased by up to two and a half times. This increase has been sustained throughout the duration of treatment (up to 250 days). To date, RG7916 remains well-tolerated at all doses and no-one has withdrawn from any RG7916 study due to drug related side effects. The information from Part 1 has allowed us to confirm the dose of RG7916 for Part 2 of SUNFISH and the first patient has been enrolled into Part 2.

https://liz-sma-blog.eu/roche-slaepper-stor-uppdatering-pa-de-tva-molekylerna-rg7916-och-olesoxime/

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Firefish Efficacy of RO7034067 in Infants With SMA Type1
Jewelfish A Study of RO7034067
Sunfish A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of RO7034067 in SMA Type 2 and 3

First Publication 29. Aug 2016 UPDATED Nils 2018-04-09

Mia

Mia

Mamma till tre barn och tvillingarna, en av tvillingarna min äldsta son har SMA Type I-II. Jag arbeta som professionell assistent inom hälso- och sjukvård

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