Evrysdi (risdiplam) in infants with Type 1 spinal muscular atrophy (SMA). Evrysdi (risdiplam) bei Babies mit Typ 1 spinale Muskelatrophie (SMA)
Tag: Spinal muscular atrophy
Det finst ingen utdrag, fordi innlegget er verna.

FDA Approves First Oral Drug of Evrysdi™ (risdiplam) for Treatment of Spinal Muscular Atrophy (SMA)