Scholar Rock announced On Track to Initiate Phase 2 Proof-of-Concept Study in Later-Onset SMA in 1Q19

Scholar Rock made transformative progress in the second quarter with the successful completion of our IPO and the initiation of the Company’s first clinical trial,” said Nagesh Mahanthappa, Ph.D, President and CEO of Scholar Rock. “We are well-positioned to continue to progress SRK-015 and build our pipeline of future product… Att fortsätt läsa

BE SMA AWARE > August is SMA Awareness Month – Augusti vara månaden då SMA uppmärksammas

  We sprayed all our positive vibs and show muscles for our weakest 💪 Spinal Muscular Atrophy is the number one genetic killer of children under two I know that wounds of losing a child never heals completely, Of course we thinking on all the parents who lost their child to… Att fortsätt läsa

SPINRAZA (nusinersen) EU label will include information on the potential risk of hydrocephalus

Biogen published the following information and address your questions and concerns about the upcoming SPINRAZA (nusinersen) EU label (Prescribing information and Package Leaflet) update that will include information on the potential risk of hydrocephalus. All medicines are evaluated for the benefit they provide to patients as well as the potential… Att fortsätt läsa

Build up finger and hand strength

I found these exercises so inspiring that we added them to our daily exercise program. Finger exercises on a guitar or ukulele. Can you guess the song???? Alex is working with a ukulele to build up finger/hand strength for the guitar. #takethatsma #specialneedsmusic #highrollers #highsonwheels @joshurban A post shared by… Att fortsätt läsa